Niagen Bioscience wins FDA rare pediatric disease designation for NB4168 in ataxia telangiectasia - NAGE News | RalliesNiagen Bioscience wins FDA rare pediatric disease designation for NB4168 in ataxia telangiectasia
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NAGE• FDA and EMA designations for NB4168
- Niagen Bioscience won FDA Rare Pediatric Disease designation for NB4168 to treat ataxia-telangiectasia.
- EMA granted orphan medicinal product designation for NB4168, supporting global clinical development incentives for the rare genetic disorder.